Clinical Trial: A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults
Study Status: Completed
Recruit Status: RECRUITING
Condition: Primary Ciliary Dyskinesia
Study Type: OBSERVATIONAL
Official Title: A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults
Brief Summary:
The goal of this observational study is to characterize clinical measures and biomarkers of airway disease in adults with primary ciliary dyskinesia (PCD) and in a group of healthy volunteers (HV) to establish normative values.Lung function, mucociliary clearance, radiological findings, and clinical findings will be assessed.Furthermore, quality of life will be assessed using QOL-PCD, a disease specific questionnaire.
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