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First received: December 19, 2022

Clinical Trial: A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults

Study Status: Completed

Recruit Status: RECRUITING

Condition: Primary Ciliary Dyskinesia

Study Type: OBSERVATIONAL


Official Title: A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults

Brief Summary: The goal of this observational study is to characterize clinical measures and biomarkers of airway disease in adults with primary ciliary dyskinesia (PCD) and in a group of healthy volunteers (HV) to establish normative values.Lung function, mucociliary clearance, radiological findings, and clinical findings will be assessed.Furthermore, quality of life will be assessed using QOL-PCD, a disease specific questionnaire.

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