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First received: January 09, 2023

Clinical Trial: A Study to Understand the Long-term Safety and Effects of an Experimental Gene Therapy for Duchenne Muscular Dystrophy.

Study Status: Completed

Recruit Status: RECRUITING

Condition: Duchenne Muscular Dystrophy

Study Type: INTERVENTIONAL


Official Title: Long-term Follow-up Safety and Efficacy Study in Participants With Duchenne Muscular Dystrophy Who Have Received Fordadistrogene Movaparvovec in a Preceding Clinical Study

Brief Summary: The purpose of this study is to understand the safety and effects of an experimental gene therapy called fordadistrogene movaparvovec.We are seeking participants from previous Pfizer interventional studies.We will follow participants' experience in this study for 10 years after the end of their previous study.Participants will have 1 annual onsite visit and a few annual remote visits.The exact number of remote visits will be decided by their study doctor.

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